TY - GEN AU - Muñoz Fernández, Pilar AU - Tristán Manzano, María AU - Sánchez Gilabert, Almudena AU - Santilli, Giorgia AU - Galy, Anne AU - Thrasher, Adrian J. AU - Martín Molina, Francisco PY - 2020 UR - http://hdl.handle.net/10481/66916 AB - Transplant of gene-modified autologous hematopoietic progenitors cells has emerged as a new therapeutic approach for Wiskott-Aldrich syndrome (WAS), a primary immunodeficiency with microthrombocytopenia and abnormal lymphoid and myeloid functions.... LA - eng PB - Elsevier TI - WAS Promoter-Driven Lentiviral Vectors Mimic Closely the Lopsided WASP Expression during Megakaryocytic Differentiation DO - 10.1016/j.omtm.2020.09.006 ER -